日韩精品久久一区二区三区_亚洲色图p_亚洲综合在线最大成人_国产中出在线观看_日韩免费_亚洲综合在线一区

Global EditionASIA 中文雙語Fran?ais
China
Home / China / Health

New hope offered to rare disease patients

By ZHOU WENTING in Shanghai | China Daily | Updated: 2021-12-14 08:18
Share
Share - WeChat
A 10-month-old patient with spinal muscular atrophy, or SMA, is taken to the hospital in Maoming, Guangdong province, in February. Provided to China Daily

Early this month, the world's first therapy to treat spinal muscular atrophy, or SMA, a rare genetic disorder that affects muscle control, was added to the National Reimbursement Drug List in China.

It was the first time that a highly expensive drug to treat a rare condition had been included on the list.

This means that most children who have SMA, which results in death in 95 percent of patients up to 18 months of age, can be saved by an injection at a far more affordable price than previously. Patients who have reached adulthood can also benefit from the therapy.

The treatment was priced at 700,000 yuan ($109,800) per dose when it was launched in China in April 2019. Official data showed that only 50 patients in the country had used it, paying the full price before the therapy was included on the national list. There are estimated to be 20,000 to 30,000 SMA patients in China.

Parents whose children have SMA said they had waited years for affordable medication, adding that it was unbelievable that their dreams had eventually come true.

Xing Huanping, executive director of the Mei'er Advocacy and Support Center for SMA, which has some 2,000 patients registered nationwide, said: "Almost all the parents burst into tears on hearing this news. This disease has put them through the mill, but finally the availability of the therapy, which once had a sky-high price, has offered them a ray of hope.

"The families are grateful to the government not giving up on this small patient community and to the pharmaceutical company's sincerity in providing the world's lowest price for the medication and choosing to stand with them," she said.

In addition to the SMA injection developed by Biogen, which is based in the United States, six other therapies to treat rare diseases have been added to the updated National Reimbursement Drug List, which takes effect next month. They include the world's first and only drug approved to treat walking impairments among patients with multiple sclerosis, which was filed with the National Medical Products Administration this year and given market approval in May.

Feng Jiamei, founder and director-general of the Mei'er center, said, "These past five years have seen tremendous developments in national policies, medical solutions and social awareness of rare diseases.

"With improved drug accessibility and affordability, we believe the plight of patients will be significantly changed. They're expected to survive with a better quality of life and be both a reduced family and economic burden."

Rare diseases have attracted increased public attention.

In 2018, China's first rare disease list, comprising 121 such diseases, was drawn up. A series of measures has also been announced to encourage research into these diseases and the development of orphan drugs-those used to treat rare medical conditions, but which are unprofitable to produce without government assistance.

1 2 3 4 Next   >>|
Top
BACK TO THE TOP
English
Copyright 1995 - . All rights reserved. The content (including but not limited to text, photo, multimedia information, etc) published in this site belongs to China Daily Information Co (CDIC). Without written authorization from CDIC, such content shall not be republished or used in any form. Note: Browsers with 1024*768 or higher resolution are suggested for this site.
License for publishing multimedia online 0108263

Registration Number: 130349
FOLLOW US
 
主站蜘蛛池模板: 亚洲一区色 | 欧美搞黄视频 | 亚洲一区二区免费视频 | 毛片a片 | 超碰8 | 久久久久99 | 91精品国产综合久久婷婷香蕉 | 日韩成人在线视频 | 久久婷婷是五月综合色狠狠 | 人人爽人人看 | 日韩a在线看免费观看视频 五月天激情视频在线观看 成人97在线观看免费高清 | 狠狠综合久久av一区二区小说 | 成年做羞羞免费观看视频网站 | 欧美精品一区在线发布 | 欧洲精品视频在线观看 | 久久天堂| 日韩中文在线 | 999国产一区二区三区四区 | 在线成人免费视频 | 成人免费毛片高清视频 | 国产99精品一区二区三区免费 | 久久综合九色综合欧美播 | 国产精品一区av | 欧美午夜色视频国产精品 | 老头天天吃我奶躁我午夜视频 | 日本免费在线视频 | 色狠狠成人综合网 | 春宵福利网站在线观看 | 我爱看片(永久免费) | 97超级碰碰碰视频在线视频观看 | 另类视频在线观看 | 亚洲视频毛片 | 国产av毛片 | 久久成人精品视频 | 波多野结衣一区二区三区88 | 日本aaaaa高清免费看 | 欧美精品色 | 欧美亚洲一区 | 嫩草国产 | 成人一区专区在线观看 | 114美女做爰视频在线 |